Research Pipeline

AlterRNA's innovative RNA therapeutics and biotech research projects

3

Total Projects

Filters

  • mRNA Therapeutics
  • Gene Editing
  • Immunotherapy
  • Oncology

  • mRNA Therapeutics
  • Gene Editing
  • Immunotherapy
  • Oncology

Showing 3 projects

MPAN: C19orf12 Protein Replacement Therapy – A Knockdown In Vitro Study

MPAN is a rare, progressive neurodegenerative disorder for which there is currently no disease-modifying treatment. Our work is focused on…

Discovery Preclinical Filing Patent Clinical Readiness
icon

Duration

18 months

icon

Team Size

6

icon

Progress

80% Complete

80% Funded

$200,000 of $250,000
Discovery Preclinical456 IND Preparation Clinical Readiness
icon

Duration

6 months

icon

Team Size

5

icon

Progress

70% Complete

60% Funded

$60,000 of $100,000

Human BBB Platform (Organ-Specific Delivery)

This research is for Human BBB platform for organ specific delivery.

Discovery Preclinical IND Preparation Clinical Readiness
icon

Duration

8 months

icon

Team Size

9 members

icon

Progress

10% Complete

60% Funded

$30,000 of $50,000
×
🕒
📝